In a context marked by pressure on public budgets and the rise of hybrid models in the social economy, donations from individuals and corporate patron represent essential financial resources for public interest structures. In France, they represented €5.4 billion and...
They're called "rare diseases." The term suggests they affect a handful of individuals, isolated cases, and medical exceptions. However, this impression is misleading. In France, more than 3 million people are affected by a rare disease. Worldwide, more than 300...
Rare diseases affect more than 3 million people in France today. Behind every child, teenager, or adult affected, there is almost always a loved one who watches over them, cares for them, supports them, and organizes their lives. These family caregivers—parents,...
Lysosomal diseases are among the least known rare diseases to the general public, yet they affect thousands of families around the world. In France, more than 3,000 cases have been recorded according to the association Vaincre les maladies lysosomales (Defeating...
Sanfilippo syndrome, also known as Mucopolysaccharidosis Type III (MPS III), is a rare genetic disorder that affects the brain. It causes a progressive decline in mental and physical abilities, leading to a loss of cognitive and motor functions. Symptoms typically...